A Phase 2, Randomized, Human Growth Hormone-Controlled, Multicenter, Basket Study of Vosoritide in Children with Turner Syndrome, Short Stature Homeobox-Containing Gene Deficiency, and Noonan Syndrome with an Inadequate Response to Human Growth Hormone
Phase 2, Randomized, Human Growth Hormone-Controlled, Multicenter, Basket Study
Turner Syndrome, Short Stature Homeobox-Containing Gene Deficiency and Noonan Syndrome
Principal Investigator