The purpose of this study is to find out if different dose levels (amounts) of the study drug are safe. This study will also measure whether the study drug improves your vision.
Currently there is no approved treatment for Retinitis Pigmesntosa due to the P23H mutation.
The study drug is designed to repair the problem that causes vision loss due to this mutation.
Main Procedures Involved: At each study visit, you will be asked about your health and several study
assessments and tests will be performed.
Duration of Participation: Your participation will last for 12 months (1 year) from the time you will receive the
study treatment. If you decide to take part in the study, you will have to visit the
study site 9 to 13 times. It is possible that some of these visits will be planned on
multiple consecutive days. You may need to stay overnight near the study site. You
may bring someone with you. In exceptional cases, e.g. related to restrictions
related to the COVID-19 pandemic, part of your visit may be performed by phone
and/or the visit at your study site may be postponed to a later date.
18 to 100 years
Treatment
Marc Mathias, MD
Protocol Number: 19-2294
More information available at ClinicalTrials.gov: NCT04123626
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