(AG348-C-023) A Phase 3, Multicenter, Randomized, Double-blind, Placebo-Controlled Study to Evaluate the Efficacy and Safety of Mitapivat in Pediatric Subjects With Pyruvate Kinase Deficiency Who Are Not Regularly Transfused, Followed by a 5-Year Open-label Extension Period
Details
Age
Child and Teen
Locations
Childrens Hospital Colorado
Principal Investigator
Taizo Nakano
Study ID
Protocol Number: 23-1651
Categories
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